Items where Author is "Bolon, B"
ROSS, P.D., GADALLA, K.K.E., THOMSON, S.R., SELFRIDGE, J., BAHEY, N.G., BENITO, J., BURSTEIN, S.R., MCMINN, R., BOLON, B., HECTOR, R.D. and COBB, S.R., 2025. Self-regulating gene therapy ameliorates phenotypes and overcomes gene dosage sensitivity in a mouse model of Rett syndrome. Science Translational Medicine, 17 (792). ISSN 1946-6234
POWERS, S., LIKHITE, S., GADALLA, K.K., MIRANDA, C.J., HUFFENBERGER, A.J., DENNYS, C., FOUST, K.D., MORALES, P., PIERSON, C.R., RINALDI, F., PERRY, S., BOLON, B., WEIN, N., COBB, S., KASPAR, B.K. and MEYER, K.C., 2023. Novel MECP2 gene therapy is effective in a multicenter study using two mouse models of Rett syndrome and is safe in non-human primates. Molecular Therapy, 31 (9), pp. 2767-2782. ISSN 1525-0016