Novel MECP2 gene therapy is effective in a multicenter study using two mouse models of Rett syndrome and is safe in non-human primates

Powers, S, Likhite, S, Gadalla, KK ORCID: https://orcid.org/0000-0002-1657-8953, Miranda, CJ, Huffenberger, AJ, Dennys, C, Foust, KD, Morales, P, Pierson, CR, Rinaldi, F, Perry, S, Bolon, B, Wein, N, Cobb, S, Kaspar, BK and Meyer, KC, 2023. Novel MECP2 gene therapy is effective in a multicenter study using two mouse models of Rett syndrome and is safe in non-human primates. Molecular Therapy, 31 (9), pp. 2767-2782. ISSN 1525-0016

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Item Type:	Journal article
Publication Title:	Molecular Therapy
Creators:	Powers, S., Likhite, S., Gadalla, K.K., Miranda, C.J., Huffenberger, A.J., Dennys, C., Foust, K.D., Morales, P., Pierson, C.R., Rinaldi, F., Perry, S., Bolon, B., Wein, N., Cobb, S., Kaspar, B.K. and Meyer, K.C.
Publisher:	Elsevier BV
Date:	6 September 2023
Volume:	31
Number:	9
ISSN:	1525-0016
Identifiers:	Number Type 10.1016/j.ymthe.2023.07.013 DOI 1807885 Other
Divisions:	Schools > School of Science and Technology
Record created by:	Laura Ward
Date Added:	25 Sep 2023 09:14
Last Modified:	25 Sep 2023 09:14
URI:	https://irep.ntu.ac.uk/id/eprint/49794

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