Items where Author is "Wein, N"

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POWERS, S., LIKHITE, S., GADALLA, K.K., MIRANDA, C.J., HUFFENBERGER, A.J., DENNYS, C., FOUST, K.D., MORALES, P., PIERSON, C.R., RINALDI, F., PERRY, S., BOLON, B., WEIN, N., COBB, S., KASPAR, B.K. and MEYER, K.C., 2023. Novel MECP2 gene therapy is effective in a multicenter study using two mouse models of Rett syndrome and is safe in non-human primates. Molecular Therapy, 31 (9), pp. 2767-2782. ISSN 1525-0016

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