Items where Author is "Wein, N"

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Journal article

POWERS, S., LIKHITE, S., GADALLA, K.K., MIRANDA, C.J., HUFFENBERGER, A.J., DENNYS, C., FOUST, K.D., MORALES, P., PIERSON, C.R., RINALDI, F., PERRY, S., BOLON, B., WEIN, N., COBB, S., KASPAR, B.K. and MEYER, K.C., 2023. Novel MECP2 gene therapy is effective in a multicenter study using two mouse models of Rett syndrome and is safe in non-human primates. Molecular Therapy, 31 (9), pp. 2767-2782. ISSN 1525-0016

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